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Ascendis因Yorvipath治疗甲状腺功能减退症获得FDA孤儿药地位

2024-09-12 06:07

  • The FDA has granted Orphan Drug Designation to Ascendis Pharma (ASND) for its prodrug Yorvipath for the treatment of hypothyroidism in adults.
  • Yorvipath is also known as palopegteriparatide and was developed as TransCon PTH. Palopegteriparatide originally received Orphan Drug Designation from the FDA in 2018.

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